Medical Writing Rare Diseases Penning hope: The impact of medical writing for rare conditions
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Volume 34, Issue 1 - Rare Diseases

Penning hope: The impact of medical writing for rare conditions

Abstract

In this article, I explain my route into the world of rare conditions, my experience of working as a clinician, and my passion for raising awareness to all involved. I achieve this by providing education to healthcare professionals, patients, and patient advocates in low- and middle-income countries. I also discuss the vital role that medical writers have played in this mission.

Medical Writing. 2025;34(1):52–54. https://doi.org/10.56012/kppv3486

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Articles

Editorial
From the Editor
Writing for rare diseases
EMWA News
Living with a rare disease: A personal perspective
Essential investments in optimising clinical research for rare disease
Regulatory writing for rare disease: An interview with Kelley Hill
Writing for orphan drugs: A compass to navigate document types and regional requirements
Innovative use of master protocols for pivotal studies in rare diseases
Model-informed drug development in rare diseases
Population diversity in clinical trials for rare diseases: A regulatory writer’s perspective
How can real-world data, registries, and databases address the challenges of rare diseases?
Penning hope: The impact of medical writing for rare conditions
An interview with Research Policy and Initiatives Director Roseline Favresse at the European Organisation for Rare Diseases
News from the EMA
Medical devices
AI/Automation
Biotechnology
My First Medical Writing
Good Writing Practice
Freelancing
The Crofter: Sustainable Communications

Links

The Write Stuff Archive Contact Instructions for Authors Article Template (Word) Journal Policies

Editoral Board

Editor-in-Chief

Raquel Billiones

Co-Editors

Evguenia Alechine

Jonathan Pitt

Managing Editor

Victoria White

Deputy Managing Editor

Alicia Brooks Waltman

Associate Editors

Anuradha Alahari

Jennifer Bell

Nicole Bezuidenhout

Claire Chang

Barbara Grossman

Sarah Milner

John Plant

Sampoorna Rappaz

Amy Whereat

Section Editors

Daniela Kamir

AI/Automation

Jennifer Bell

Biotechnology

Nicole Bezuidenhout 

Digital Communication

Somsuvro Basu

EMWA News 

Adriana Rocha

Freelancing

Ana Sofia Correia 

Gained in Translation

Ivana Turek

Getting Your Foot in the Door

Wendy Kingdom / Amy Whereat

Good Writing Practice

Pablo Izquierdo / Alison McIntosh 

In the Bookstores

Maria Kołtowska-Häggström

Lingua Franca and Beyond

Maddy Dyer

Publications

Lisa Chamberlain-James

Medical Communications/Writing for Patients

Payal Bhatia

Medical Devices

Evguenia Alechine

My First Medical Writing

Anuradha Alahari

News from the EMA

Tiziana von Bruchhausen

Pharmacovigilance

Clare ChangZuo Yen Lee 

Regulatory Matters

Sam Hamilton

Regulatory Public Disclosure

Louisa Ludwig-Begall / Sarah Kabani

The Crofter: Sustainable Communications

Jeff Blair / Luiza Ventura

Veterinary Writing

Editors Emeritus

Elise Langdon-Neuner

Phil Leventhal

Layout Designer

Chris Monk